Orphan Drugs for Rare Diseases 2018


On 24 & 25 September 2018, Seoul (South Korea) will host the BioTech Pharma Summit: Orphan Drugs for Rare Diseases 2018 conference. This year’s event will bring together government, hospitals, pharmaceuticals, biopharmaceuticals, non-profit organisations, orphan drugs developers as well as regional and local manufacturers. We are putting together an agenda that address the driving macroeconomic factors, policies and issues that will steer the development of orphan drugs globally including commercialisation, policies, reimbursement, pricing and more.

Orphan Drugs for Rare Diseases 2018 features more than 20 speakers from FDA, EMA, NIH and the orphan product industry, more than 80 thought leaders from the patient community and industry, will provide a unique opportunity to hear from the experts and join the conversation on issues of unprecedented importance.


With the global Orphan Drug market expected to grow to $127 billion by 2018-2019, and another Rare Disease Day just having passed, there is a constantly growing awareness and interest for this industry, enabling more research to make a difference in patients’ lives. Orphan Drugs for Rare Diseases 2018 conference will bring together some of the leading senior industry professionals to network, learn, and discuss current issues in the rare disease industry.

Orphan Drugs for Rare Diseases 2018 has evolved from a one track conference focused on regulatory pathways, policy and incentives, to a global gathering of 200+ leaders in orphan drugs from 30+ countries and over 20+ presentations and case studies covering all aspects of orphan drug development and rare disease research.


The BioTech Pharma Summit: Orphan Drugs for Rare Diseases 2018 will help connect industry professionals internationally, ensuring there is a great networking and learning opportunity to share knowledge of research, developments and issues. With topics being discussed such as Cell and Gene Therapy; Patient Recruitment and Patient-centric Research; Clinical Development, Regulatory Guidelines; Strategic Partnerships; Pricing and Reimbursement; and many more, this year’s conference promises to be the perfect platform to exchange knowledge and network with your peers!



  • Future Outlook for Patient Assistance Programs
  • Challenges, Opportunities And Treatment Of Rare Diseases
  • Current Topics from the FDA
  • Cutting-edge science and tech to enhance rare diseases research, diagnosis and therapeutics
  • Novel drug modalities, assays & models, therapeutic strategies
  • Successful patient recruitment and project delivery in rare indications
  • The Challenge of Healthcare Costs and Treatment Prices
  • Sustaining Orphan Drug Development and Availability
  • Developing a state of art telemedicine rare disease service
  • Novel approaches for the genetic therapy of rare diseases
  • Artificial intelligence to advance rare disease treatments
  • Employee wellbeing & health in relation to office design
  • Investor Perspective: The Outlook for Investment in Orphan Products
  • Emerging approaches for effective, fast, affordable and successful orphan drugs development
  • Rare Disease Drug, Biologic and Device Development: Achievements and Opportunities
  • Global Orphan Drug Regulatory Strategy
  • Drug repurposing for rare diseases
  • Insights into regulatory, pricing, reimbursement, commercialization, market access for rare disorders drugs


The BioTech Pharma Summit (EPM Group) are exclusive events consisting of world-class keynote addresses and presentations designed specifically for senior level attendees from research & academic institutions, clinical research institutions and hospital laboratories as well as major pharmaceutical and biotech companies based Worldwide. Delegates typically include CEOs, VPs, Drug developers, Academics and Researchers, CROs, Scientists and Medical Doctors of:

  • Drug Discovery & Development
  • Personalized Medicine
  • Translational Medicine
  • Experimental Medicine
  • Innovative Medicine
  • Stratified Medicine
  • Regenerative Medicine
  • Cell / Molecular Biology
  • Molecular Diagnostics
  • Diagnostic Development
  • Cell / Gene Therapy
  • Targeted Therapy
  • Rare & ultra-rare Diseases
  • Genetic Diseases
  • Metabolic & Gastrointestinal (GI) disorders
  • Haematology
  • Immunology
  • Non-Hodgkin Lymphoma
  • Acute Myeloid Leukemia
  • Cystic Fibrosis
  • Glioma
  • Pancreatic Cancer
  • Ovarian Cancer
  • Multiple Myeloma
  • Duchenne Muscular Dystrophy
  • Graft vs Host Disease
  • Renal Cell Carcinoma
  • Clinical Research / Trials / Development
  • Neurology, mental health, neuromuscular and musculoskeletal disorder
  • Dermatology, ophthalmology, urology and nephrology Immunology
  • Endocrinology
  • Cardiovascular, pulmonological disorders
  • Cancer / Oncology
  • Market Access
  • Pricing & Reimbursement
  • Alliance Management
  • Patient Advocacy
  • n-Licensing/Out-Licensing
  • Regulatory & Medical Affairs
  • Commercial Development
  • Health Economics/Outcomes Research (HEOR)
  • Orphan Foundations/Associations
  • Bioinformatics
  • Big Data
  • Digital Health
Basic Package
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Access to all Sessions

Access to all Networking Sessions

Cocktail Reception Included

Premium Package
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Unique one-on-one meetings

Airport pick-up/drop-off

2 nights at the Hotel Venue

Basic Exhibition Package
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3m2 exhibition space

1 Complementary ticket

25% discount for extra ticket

Premium Exhibition Package
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6m2 exhibition space

1 Complementary ticket

2 nights at the Hotel Venue